Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...
Gene therapy represents a paradigm shift in modern medicine, offering unprecedented opportunities to combat diseases at their ...
The company raised $200 million after early findings hinted its therapy could be more potent than others like it, including ...
A revolutionary gene therapy treatment in London has improved the vision of children suffering from a rare genetic disorder, ...
A new inhalable gene therapy for cystic fibrosis (CF) has entered Phase I clinical trials, a major milestone on the journey ...
The American Cancer Society estimates that 83,000 new cases of bladder cancer will be diagnosed this year, with almost 17,000 ...
HHS Secretary Robert F. Kennedy Jr. is preparing to remove committee members who advise the government on vaccine approvals ...
Researchers have identified a gene therapy that could prevent life-threatening arrhythmias by restoring the heart’s ...