Batten disease is a rare genetic disorder affecting 3 in 100,000 babies in the U.S., causing neurodegeneration, seizures, ...

Toddlers who were born with the most severe form of childhood blindness can now see after groundbreaking gene therapy ...

Children with rare eye condition receive pioneering gene therapy in UK to preserve eyesightSource: PA The former couple ...

Dr. Chandler Park discusses the importance of genetic testing and personalized care in patients with genitourinary cancers.

Four young children have gained life-changing improvements in sight following treatment with a pioneering new genetic medicine through UCL Institute of Ophthalmology and Moorfields Eye Hospital, with ...

At the Envision Summit 2025 in San Juan, Puerto Rico, Mike Farkas, MD, discussed gene therapy research for retinal ...

Jaime Bortz, 39, is losing her memory to dementia. Her mom, now a full-time carer, is foreshadowing the burden many families will experience as dementia cases rise.

Senate committee members heard arguments on a bill that would place a 10-year pause on administering mRNA vaccines in Idaho on Monday but did not take a vote.

Cash-strapped gene-therapy company Bluebird bio agreed to be acquired by private-equity firms Carlyle Group and SK Capital Partners in a deal potentially worth up to $96 million.